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Phase 3 (105 companies)

Companies with at least one active program at Phase 3.

Ticker Company Therapeutic areas Phase 3 programs Lead stage Mkt cap Programs
FDMT 4D Molecular Therapeutics OphthalmologyRespiratory Rare 2 Phase 3 $677M 5
AARD Aardvark Therapeutics DermatologyMetabolic+1 Rare 1 Phase 3 $25.6M 3
ABVX Abivax Immunology 1 Phase 3 $7.50B 2
ACIU AC Immune Neurology Rare 1 Phase 3 $222M 11
ALDX Aldeyra Therapeutics DermatologyOncology+1 2 NDA Submitted $38.3M 5
ALT Altimmune GI/HepatologyMetabolic+1 1 Phase 3 $405M 3
AMLX Amylyx Pharmaceuticals MetabolicNeurology Rare 1 Phase 3 $3.79B 5
ANAB AnaptysBio DermatologyGI/Hepatology+2 Rare 2 Approved $1.39B 9
ANNX Annexon HematologyNeurology+2 Rare 2 Phase 3 $796M 6
RCUS Arcus Biosciences DermatologyImmunology+1 3 Phase 3 $2.63B 8
ARDX Ardelyx GI/HepatologyRenal 1 Approved $724M 4
AXSM Axsome Therapeutics Neurology Rare 6 Approved $6.96B 15
BLTE Belite Bio MetabolicOphthalmology Rare 1 NDA Submitted $6.21B 6
BCRX Biocryst Pharmaceuticals DermatologyImmunology+1 Rare 1 Approved $1.98B 4
BCTX BriaCell Therapeutics Oncology 1 Phase 3 $34.5M 8
CADL Candel Therapeutics Oncology 2 Phase 3 $670M 4
CRDL Cardiol Therapeutics Cardiovascular Rare 1 Phase 3 $121M 4
RNAC Cartesian Therapeutics ImmunologyNeurology+1 Rare 1 Phase 3 $230M 4
CLDX Celldex Therapeutics DermatologyImmunology+1 4 Phase 3 $2.35B 9
CGEN Compugen Oncology 4 Phase 3 $186M 7
CRVS Corvus Pharmaceuticals DermatologyOncology+1 Rare 1 Phase 3 $889M 7
CRNX Crinetics Pharmaceuticals MetabolicOncology Rare 2 Approved — 6
DFTX Definium Therapeutics Neurology 2 Phase 3 $4.47B 4
IRON Disc Medicine GI/HepatologyHematology+2 Rare 2 Phase 3 $3.59B 9
DYN Dyne Therapeutics MetabolicNeurology Rare 1 NDA Submitted $3.39B 10
EXEL Exelixis CardiovascularOncology 3 Approved $17.0B 23
EYPT EyePoint Ophthalmology 1 Phase 3 $31.0M 2
FBIO Fortress Biotech DermatologyHematology+3 Rare 2 Approved $61.7M 12
GUTS Fractyl Health Metabolic 1 Phase 3 — 1
GNLX Genelux Oncology 1 Phase 3 $88.7M 3
GERN Geron Oncology 1 Approved $638M 3
GOSS Gossamer Bio Cardiovascular Rare 1 NDA Submitted — 4
GLSI Greenwich LifeSciences Oncology 1 Phase 3 $223M 1
HRMY Harmony Biosciences MetabolicNeurology Rare 4 Approved $1.94B 17
HROW Harrow Ophthalmology Rare 2 Approved $1.01B 15
HELP Helus Pharma Neurology 1 Phase 3 $655M 3
IDYA IDEAYA Biosciences Oncology 1 NDA Submitted $3.02B 14
IMTX Immatics Oncology 1 Phase 3 $968M 8
IMRX Immuneering Oncology 1 Phase 3 $238M 5
IMUX Immunic GI/HepatologyNeurology 1 Phase 3 $106M 4
IMCR Immunocore DermatologyInfectious Disease+2 3 Approved $1.60B 15
IMVT Immunovant ImmunologyNeurology Rare 1 Phase 3 $6.31B 5
INMB Inmune Bio Dermatology Rare 1 Phase 3 $35.0M 1
INSM Insmed CardiovascularImmunology+3 Rare 2 Approved $25.1B 15
NTLA Intellia Therapeutics CardiovascularImmunology Rare 2 NDA Submitted $1.59B 3
IVVD Invivyd Infectious Disease 1 Approved $166M 5
IONS Ionis Pharmaceuticals CardiovascularHematology+5 Rare 12 Approved $6.55B 29
KROS Keros Therapeutics NeurologyOncology Rare 2 Phase 3 $184M 5
KPRX Kiora Pharmaceuticals Ophthalmology Rare 1 Phase 3 $6.4M 4
KOD Kodiak Sciences Ophthalmology 6 Phase 3 $6.24B 8
KYTX Kyverna Therapeutics ImmunologyNeurology+1 Rare 1 NDA Submitted $302M 7
LBRX LB Pharmaceuticals Neurology 1 Phase 3 $1.36B 3
LQDA Liquidia CardiovascularImmunology+1 Rare 2 Approved $3.97B 9
MAIA MAIA Biotechnology Oncology 1 Phase 3 $64.5M 7
MGTX MeiraGTx ImmunologyMetabolic+2 Rare 1 Phase 3 $864M 16
MESO Mesoblast CardiovascularGI/Hepatology+2 Rare 2 Approved $1.85B 5
MIST Milestone Pharmaceuticals Cardiovascular 1 Approved $95.0M 2
MLTX MoonLake Immunotherapeutics DermatologyImmunology Rare 1 NDA Submitted $981M 4
NKTR Nektar Therapeutics DermatologyImmunology+2 1 Phase 3 $1.27B 11
NGEN NervGen Pharma Neurology 1 Phase 3 $143M 3
NGNE Neurogene Neurology Rare 1 Phase 3 $506M 1
NAMS NewAmsterdam Pharma CardiovascularMetabolic+1 2 NDA Submitted $2.27B 6
NRIX Nurix Therapeutics ImmunologyNeurology+1 2 Phase 3 $1.67B 13
NVCT Nuvectis Pharma HematologyOncology+1 Rare 2 Phase 3 $719M 9
OCGN Ocugen Infectious DiseaseOphthalmology Rare 4 Phase 3 $314M 12
OCS Oculis Holding NeurologyOphthalmology Rare 1 Phase 3 $417M 5
OLMA Olema Pharmaceuticals Oncology 1 Phase 3 $641M 3
IRD Opus Genetics Ophthalmology Rare 2 Approved $348M 12
ORIC Oric Pharmaceuticals Oncology 1 Phase 3 $914M 5
OTLK Outlook Therapeutics Ophthalmology 2 Approved $106M 3
PTN Palatin Technologies ImmunologyMetabolic+1 Rare 1 Phase 3 $11.2M 8
PTGX Protagonist Therapeutics DermatologyHematology+2 Rare 3 Approved $8.62B 12
RAPP Rapport Therapeutics Neurology 1 Phase 3 $1.45B 10
RLAY Relay Therapeutics DermatologyOncology Rare 1 Approved $4.11B 4
RVPH Reviva Pharmaceuticals CardiovascularDermatology+2 Rare 1 Phase 3 $4.8M 10
RVMD Revolution Medicines Oncology 4 Approved $41.6B 11
RYTM Rhythm Pharmaceuticals Metabolic Rare 5 Approved $7.78B 14
SGMT Sagimet Biosciences DermatologyMetabolic 1 Phase 3 $698M 3
SRPT Sarepta Therapeutics NeurologyRespiratory Rare 1 Approved $1.91B 11
SLS SELLAS Life Sciences Group Oncology 1 Phase 3 $1.70B 9
SLDB Solid Biosciences CardiovascularNeurology Rare 1 Phase 3 $736M 6
STOK Stoke Therapeutics Neurology Rare 1 Phase 3 $1.74B 2
GPCR Structure Therapeutics MetabolicRespiratory Rare 2 Phase 3 $4.35B 5
SMMT Summit Therapeutics Oncology 3 NDA Submitted $13.1B 6
TSHA Taysha Gene Therapies Neurology Rare 1 Phase 3 $1.41B 4
TLX Telix Pharmaceuticals Oncology 4 Approved $3.27B 25
TENX Tenax Therapeutics Cardiovascular Rare 1 Phase 3 $77.0M 2
TGTX Tg Therapeutics Neurology Rare 1 Approved $9.16B 6
TVTX Travere Therapeutics MetabolicRenal Rare 1 Approved $4.76B 7
HURA TuHURA Biosciences Oncology 1 Phase 3 $104M 4
RARE Ultragenyx Pharmaceutical CardiovascularMetabolic+1 Rare 2 Approved $1.57B 10
VNDA Vanda Pharmaceuticals CardiovascularDermatology+6 Rare 8 Approved $231M 27
PCVX Vaxcyte Infectious Disease 2 Phase 3 $10.1B 7
VRCA Verrica Pharmaceuticals DermatologyOncology 1 Approved $54.8M 3
VKTX Viking Therapeutics MetabolicNeurology Rare 2 Phase 3 $3.42B 9
VIR Vir Biotechnology Infectious DiseaseOncology Rare 1 Phase 3 $2.09B 12
VRDN Viridian Therapeutics ImmunologyOphthalmology 1 Approved $3.24B 7
VOR Vor Biopharma ImmunologyNeurology Rare 2 Phase 3 $1.22B 2
VTVT vTv Therapeutics HematologyMetabolic+1 Rare 1 Phase 3 $84.4M 9
XFOR X4 Pharmaceuticals — 1 Approved $325M 2
XNCR Xencor ImmunologyNeurology+1 Rare 1 Approved $2.68B 28
XENE Xenon Pharmaceuticals Neurology Rare 3 NDA Submitted $3.79B 9
ZBIO Zenas BioPharma DermatologyImmunology+2 Rare 2 NDA Submitted $1.92B 11
ZNTL Zentalis Pharmaceuticals Oncology 1 Phase 3 $123M 1
ZYME Zymeworks OncologyRespiratory 1 Approved $2.10B 11