HomePhases › Phase 3

Phase 3 (81 companies)

Companies with at least one active program at Phase 3.

Ticker Company Therapeutic areas Phase 3 programs Lead stage Programs
FDMT 4D Molecular Therapeutics OphthalmologyRespiratory Rare 1 Phase 3 5
ACIU AC Immune Neurology Rare 1 Phase 3 10
ALDX Aldeyra Therapeutics DermatologyOncology+1 Rare 2 NDA Submitted 7
ALT Altimmune GI/HepatologyMetabolic+1 1 Phase 3 3
AMLX Amylyx Pharmaceuticals MetabolicNeurology Rare 1 Phase 3 5
ANAB AnaptysBio DermatologyGI/Hepatology+2 Rare 1 Approved 6
ANNX Annexon HematologyNeurology+2 Rare 2 Phase 3 6
RCUS Arcus Biosciences DermatologyImmunology+1 3 Phase 3 6
ARDX Ardelyx GI/HepatologyRenal 1 Approved 4
BLTE Belite Bio MetabolicOphthalmology Rare 1 NDA Submitted 6
BCRX Biocryst Pharmaceuticals DermatologyImmunology+1 Rare 1 Approved 4
BCTX BriaCell Therapeutics Oncology 1 Phase 3 7
CRDL Cardiol Therapeutics Cardiovascular Rare 1 Phase 3 4
RNAC Cartesian Therapeutics ImmunologyNeurology+1 Rare 1 Phase 3 4
CLDX Celldex Therapeutics DermatologyImmunology+1 3 Phase 3 7
CLNN Clene Neurology Rare 1 Phase 3 5
CGEN Compugen Oncology 4 Phase 3 7
CRVS Corvus Pharmaceuticals DermatologyOncology 1 Phase 3 4
CRNX Crinetics Pharmaceuticals MetabolicOncology Rare 2 Approved 6
HELP Cybin Neurology 1 Phase 3 3
DFTX Definium Therapeutics Neurology 2 Phase 3 4
DYN Dyne Therapeutics MetabolicNeurology Rare 1 NDA Submitted 10
EXEL Exelixis CardiovascularOncology 2 Approved 22
EYPT EyePoint Ophthalmology 2 Phase 3 3
FBIO Fortress Biotech DermatologyHematology+2 Rare 1 Approved 12
GUTS Fractyl Health Metabolic 1 Phase 3 3
GNLX Genelux Oncology 1 Phase 3 3
GERN Geron Oncology 1 Approved 3
GOSS Gossamer Bio Cardiovascular Rare 2 Phase 3 4
GLSI Greenwich LifeSciences Oncology 1 Phase 3 1
HRMY Harmony Biosciences MetabolicNeurology Rare 4 Approved 17
IDYA IDEAYA Biosciences Oncology 1 NDA Submitted 13
IMRX Immuneering Oncology 1 Phase 3 5
IMUX Immunic GI/HepatologyNeurology 1 Phase 3 4
IMCR Immunocore DermatologyInfectious Disease+2 2 Approved 11
IMVT Immunovant ImmunologyNeurology Rare 1 Phase 3 6
INSM Insmed CardiovascularImmunology+2 Rare 2 Approved 17
NTLA Intellia Therapeutics CardiovascularImmunology Rare 2 NDA Submitted 3
IONS Ionis Pharmaceuticals CardiovascularHematology+5 Rare 12 Approved 29
KOD Kodiak Sciences Ophthalmology 6 Phase 3 8
KYTX Kyverna Therapeutics ImmunologyNeurology+1 Rare 1 NDA Submitted 7
MAIA MAIA Biotechnology Oncology 1 Phase 3 7
MIST Milestone Pharmaceuticals Cardiovascular 1 Approved 2
MLTX MoonLake Immunotherapeutics DermatologyImmunology Rare 2 Phase 3 4
NKTR Nektar Therapeutics DermatologyImmunology+2 1 Phase 3 11
NGNE Neurogene Neurology Rare 1 Phase 3 1
NAMS NewAmsterdam Pharma CardiovascularMetabolic+1 2 NDA Submitted 6
NRIX Nurix Therapeutics ImmunologyNeurology+1 1 Phase 3 16
NVCT Nuvectis Pharma HematologyOncology+1 Rare 2 Phase 3 8
OCGN Ocugen Infectious DiseaseOphthalmology Rare 4 Phase 3 12
OCS Oculis Holding NeurologyOphthalmology Rare 1 Phase 3 4
IRD Opus Genetics Ophthalmology Rare 2 Approved 12
OTLK Outlook Therapeutics Ophthalmology 2 Approved 3
PTN Palatin Technologies ImmunologyMetabolic+1 Rare 1 Phase 3 8
RLAY Relay Therapeutics DermatologyOncology Rare 1 NDA Submitted 5
RVPH Reviva Pharmaceuticals CardiovascularDermatology+2 Rare 1 Phase 3 10
RVMD Revolution Medicines Oncology 3 Approved 10
RYTM Rhythm Pharmaceuticals Metabolic Rare 5 Approved 13
SRPT Sarepta Therapeutics NeurologyRespiratory Rare 1 Approved 10
SLS SELLAS Life Sciences Group Oncology 1 Phase 3 9
SLDB Solid Biosciences CardiovascularNeurology Rare 1 Phase 3 6
GPCR Structure Therapeutics MetabolicRespiratory Rare 2 Phase 3 5
SMMT Summit Therapeutics Oncology 3 NDA Submitted 5
TSHA Taysha Gene Therapies Neurology Rare 1 Phase 3 4
TENX Tenax Therapeutics Cardiovascular Rare 1 Phase 3 2
TGTX Tg Therapeutics Neurology Rare 1 Approved 6
TVTX Travere Therapeutics MetabolicRenal Rare 1 Approved 7
RARE Ultragenyx Pharmaceutical CardiovascularGI/Hepatology+2 Rare 3 Approved 12
VNDA Vanda Pharmaceuticals CardiovascularDermatology+6 Rare 8 Approved 27
PCVX Vaxcyte Infectious Disease 2 Phase 3 6
VRCA Verrica Pharmaceuticals DermatologyOncology 1 Approved 3
VKTX Viking Therapeutics MetabolicNeurology Rare 2 Phase 3 8
VIR Vir Biotechnology Infectious DiseaseOncology Rare 1 Phase 3 10
VRDN Viridian Therapeutics ImmunologyOphthalmology 1 Approved 5
VOR Vor Biopharma ImmunologyNeurology Rare 2 Phase 3 2
VTVT vTv Therapeutics MetabolicRespiratory Rare 1 Phase 3 8
XNCR Xencor HematologyImmunology+4 Rare 2 Approved 36
XENE Xenon Pharmaceuticals Neurology Rare 3 NDA Submitted 9
ZBIO Zenas BioPharma DermatologyImmunology+2 Rare 2 NDA Submitted 11
ZNTL Zentalis Pharmaceuticals Oncology 1 Phase 3 1
ZYME Zymeworks OncologyRespiratory 1 Approved 11