lonvo-z lonvoguran ziclumeran · NTLA-2002 Gene Therapy Target: KLKB1 Hereditary Angioedema NDA Submitted intravenous
nex-z nexiguran ziclumeran · NTLA-2001 Gene Therapy Target: TTR Transthyretin Amyloidosis with Cardiomyopathy Phase 3 intravenous Regeneron Hereditary Transthyretin Amyloidosis with Polyneuropathy Phase 3 intravenous Regeneron
nexiguran ziclumeran NTLA-2001 · nex-z Gene Therapy Target: TTR ATTR Amyloidosis with Cardiomyopathy Phase 3 intravenous Regeneron Pharmaceuticals Hereditary ATTR Amyloidosis with Polyneuropathy Phase 3 intravenous Regeneron Pharmaceuticals