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TTR (2 companies · 6 programs)

Companies with an active program directed at TTR.

IONIS PHARMACEUTICALS INC IONS

  • WAINUA — Hereditary Transthyretin-Mediated Amyloid Polyneuropathy Approved
  • WAINUA — Transthyretin-Mediated Amyloid Cardiomyopathy Phase 3
  • TEGSEDI — Hereditary Transthyretin-Mediated Amyloid Polyneuropathy Approved
  • WAINUA — Transthyretin Amyloid Cardiomyopathy Phase 3

Intellia Therapeutics, Inc. NTLA

  • nexiguran ziclumeran — Transthyretin Amyloidosis with Cardiomyopathy Phase 3
  • nexiguran ziclumeran — Hereditary Transthyretin Amyloidosis with Polyneuropathy Phase 3