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ATTR Amyloidosis (2 companies)

Companies with an active program in ATTR Amyloidosis.

Ticker Company Therapeutic areas Programs Lead stage Mkt cap Programs
NTLA Intellia Therapeutics CardiovascularImmunology Rare 2 NDA Submitted $1.59B 3
IONS Ionis Pharmaceuticals CardiovascularHematology+5 Rare 3 Approved $6.55B 29