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Neurology (85 companies · 63 conditions)

Conditions

Amyotrophic Lateral Sclerosis 16 Rare Multiple Sclerosis 15 Alzheimer's Disease 14 Parkinson's Disease 13 Major Depressive Disorder 12 Duchenne Muscular Dystrophy 9 Rare Epilepsy 8 Myasthenia Gravis 7 Rare Schizophrenia 7 Bipolar Disorder 6 Frontotemporal Dementia 5 Rare Generalized Anxiety Disorder 5 Huntington's Disease 5 Rare Friedreich's Ataxia 4 Rare Lewy Body Dementia 4 Multiple System Atrophy 4 Rare Myotonic Dystrophy 4 Rare Attention Deficit Hyperactivity Disorder 3 Autism Spectrum Disorder 3 Chronic Pain 3 Dravet Syndrome 3 Rare Migraine 3 Post-Traumatic Stress Disorder 3 Rett Syndrome 3 Rare Substance Use Disorder 3 Facioscapulohumeral Muscular Dystrophy 2 Rare Infantile Spasms 2 Rare Narcolepsy 2 Rare Progressive Supranuclear Palsy 2 Rare Spinal Cord Injury 2 Stiff Person Syndrome 2 Rare Tourette Syndrome 2 Acute Pain 1 Aneurysmal Subarachnoid Hemorrhage 1 Angelman Syndrome 1 Rare Anorexia Nervosa 1 Charcot-Marie-Tooth Disease Type 2S 1 Rare Chronic Inflammatory Demyelinating Polyneuropathy 1 Rare Chronic Low Back Pain 1 CLN2 Batten Disease 1 Rare Cocaine Use Disorder 1 Delayed Sleep Phase Disorder 1 Dementia-Related Psychosis 1 Essential Tremor 1 Fragile X Syndrome 1 Rare Giant Axonal Neuropathy 1 Rare GNE Myopathy 1 Rare Guillain-Barré Syndrome 1 Insomnia 1 Ischemic Stroke 1 Jet Lag Disorder 1 Lennox-Gastaut Syndrome 1 Rare Limb-Girdle Muscular Dystrophy 1 Rare Motion Sickness 1 Non-24-Hour Sleep-Wake Disorder 1 Non-Fluent Variant Primary Progressive Aphasia 1 Rare Primary Periodic Paralysis 1 Rare Smith-Magenis Syndrome 1 Rare Spinal Bulbar Muscular Atrophy 1 Rare Spinal Muscular Atrophy 1 Rare Spinocerebellar Ataxia 1 Rare Tuberous Sclerosis Complex 1 Rare X-Linked Adrenoleukodystrophy 1 Rare

Companies

Ticker Company Therapeutic areas In Neurology Lead stage Mkt cap Programs
AARD Aardvark Therapeutics DermatologyMetabolic+1 Rare 1 Phase 3 $25.6M 3
ACIU AC Immune Neurology Rare 10 Phase 3 $222M 11
ABOS Acumen Pharmaceuticals Neurology 4 Phase 2 $16.2M 4
ACET Adicet Bio ImmunologyNeurology+2 Rare 1 Phase 1 $28.6M 8
ATHE Alterity Therapeutics Neurology Rare 2 Phase 2 $46.4M 2
ALT Altimmune GI/HepatologyMetabolic+1 1 Phase 3 $405M 3
AMLX Amylyx Pharmaceuticals MetabolicNeurology Rare 1 Phase 3 $3.79B 5
ANNX Annexon HematologyNeurology+2 Rare 3 Phase 3 $796M 6
ARVN Arvinas NeurologyOncology Rare 3 Approved $420M 10
ATAI Atai Beckley Neurology 5 Phase 2 $2.73B 5
AUTL Autolus Therapeutics HematologyImmunology+3 Rare 1 Approved $341M 12
AXSM Axsome Therapeutics Neurology Rare 10 Approved $6.96B 15
CABA Cabaletta Bio DermatologyImmunology+2 Rare 1 Phase 2 $280M 8
CAPR Capricor Therapeutics Infectious DiseaseNeurology Rare 1 NDA Submitted $523M 2
RNAC Cartesian Therapeutics ImmunologyNeurology+1 Rare 1 Phase 3 $230M 4
CRVO CervoMed Neurology Rare 4 Phase 2 $21.5M 4
CING Cingulate Neurology 1 NDA Submitted $61.9M 1
CLNN Clene Neurology Rare 3 NDA Submitted $56.9M 5
CGTX Cognition Therapeutics Neurology 2 Phase 2 $65.3M 2
CMPS COMPASS Pathways Neurology 3 NDA Submitted $1.22B 3
CTNM Contineum Therapeutics NeurologyRespiratory Rare 3 Phase 2 $374M 4
COYA Coya Therapeutics Neurology Rare 2 Phase 2 $70.1M 6
CYDY CytoDyn NeurologyOncology 1 Phase 2 $338M 3
DFTX Definium Therapeutics Neurology 4 Phase 3 $4.47B 4
DYN Dyne Therapeutics MetabolicNeurology Rare 7 NDA Submitted $3.39B 10
ELDN Eledon Pharmaceuticals ImmunologyMetabolic+1 Rare 1 Phase 2 $212M 3
ETON Eton Pharmaceuticals GI/HepatologyInfectious Disease+3 Rare 2 Approved $1.63B 17
EVMN Evommune DermatologyImmunology+1 1 Phase 2 $241M 6
GANX Gain Therapeutics MetabolicNeurology Rare 4 Phase 1 $45.0M 5
GHRS GH Research NeurologyWomen's Health 3 Phase 2 $1.28B 4
GRCE Grace Therapeutics Neurology 1 NDA Submitted $38.9M 1
HRMY Harmony Biosciences MetabolicNeurology Rare 12 Approved $1.94B 17
HELP Helus Pharma Neurology 3 Phase 3 $655M 3
IMUX Immunic GI/HepatologyNeurology 2 Phase 3 $106M 4
IMVT Immunovant ImmunologyNeurology Rare 2 Phase 3 $6.31B 5
IXHL Incannex Healthcare NeurologyRespiratory 1 Phase 2 $28.1M 2
INSM Insmed CardiovascularImmunology+3 Rare 2 Approved $25.1B 15
IONS Ionis Pharmaceuticals CardiovascularHematology+5 Rare 7 Approved $6.55B 29
KZIA Kazia Therapeutics NeurologyOncology Rare 1 Phase 2 $82.0M 13
KROS Keros Therapeutics NeurologyOncology Rare 2 Phase 3 $184M 5
KYTX Kyverna Therapeutics ImmunologyNeurology+1 Rare 3 NDA Submitted $302M 7
LRMR Larimar Therapeutics Neurology Rare 1 NDA Submitted $248M 1
LBRX LB Pharmaceuticals Neurology 3 Phase 3 $1.36B 3
LXEO Lexeo Therapeutics CardiovascularNeurology Rare 9 Phase 2 $237M 12
LCTX Lineage Cell Therapeutics MetabolicNeurology+1 Rare 1 Phase 2 $258M 12
LGVN Longeveron CardiovascularMetabolic+1 Rare 1 Phase 2 $5.8M 4
MPLT MapLight Therapeutics Neurology 4 Phase 2 $385M 6
MGTX MeiraGTx ImmunologyMetabolic+2 Rare 2 Phase 3 $864M 16
MESO Mesoblast CardiovascularGI/Hepatology+2 Rare 2 Approved $1.85B 5
NGEN NervGen Pharma Neurology 3 Phase 3 $143M 3
NGNE Neurogene Neurology Rare 1 Phase 3 $506M 1
NRSN NeuroSense Therapeutics Neurology Rare 3 Phase 2 $3.2M 3
NAMS NewAmsterdam Pharma CardiovascularMetabolic+1 1 NDA Submitted $2.27B 6
NKTX Nkarta ImmunologyNeurology+1 Rare 1 Phase 1 $124M 8
NRXP NRX Pharmaceuticals Neurology Rare 6 Approved $103M 7
NRIX Nurix Therapeutics ImmunologyNeurology+1 1 Phase 3 $1.67B 13
OCS Oculis Holding NeurologyOphthalmology Rare 1 Phase 3 $417M 5
OMER Omeros HematologyNeurology+2 Rare 2 Approved $1.22B 6
OVID Ovid Therapeutics Neurology Rare 3 Phase 2 $557M 4
KTTA Pasithea Therapeutics NeurologyOncology Rare 2 Phase 1 $19.3M 4
PEPG PepGen Neurology Rare 1 Phase 2 $171M 1
DTIL Precision Biosciences Infectious DiseaseMetabolic+1 Rare 2 Phase 1 $296M 5
PCSA Processa Pharmaceuticals GI/HepatologyImmunology+2 Rare 1 Phase 2 $5.4M 7
PMN ProMIS Neurosciences Neurology Rare 6 Phase 1 $37.3M 6
PRQR ProQR Therapeutics MetabolicNeurology Rare 1 Phase 1 $191M 7
RAPP Rapport Therapeutics Neurology 6 Phase 3 $1.45B 10
RLMD Relmada Therapeutics MetabolicNeurology+1 Rare 2 Phase 2 $416M 4
RVPH Reviva Pharmaceuticals CardiovascularDermatology+2 Rare 7 Phase 3 $4.8M 10
SRPT Sarepta Therapeutics NeurologyRespiratory Rare 10 Approved $1.91B 11
SLDB Solid Biosciences CardiovascularNeurology Rare 2 Phase 3 $736M 6
STOK Stoke Therapeutics Neurology Rare 1 Phase 3 $1.74B 2
TSHA Taysha Gene Therapies Neurology Rare 3 Phase 3 $1.41B 4
TGTX Tg Therapeutics Neurology Rare 6 Approved $9.16B 6
TLSA Tiziana Life Sciences ImmunologyNeurology Rare 4 Phase 2 $87.8M 5
RARE Ultragenyx Pharmaceutical CardiovascularMetabolic+1 Rare 1 Approved $1.57B 10
QURE uniQure HematologyMetabolic+1 Rare 2 Approved $1.52B 4
VNDA Vanda Pharmaceuticals CardiovascularDermatology+6 Rare 16 Approved $231M 27
VKTX Viking Therapeutics MetabolicNeurology Rare 1 Phase 3 $3.42B 9
VOR Vor Biopharma ImmunologyNeurology Rare 1 Phase 3 $1.22B 2
VYGR Voyager Therapeutics MetabolicNeurology Rare 8 Phase 1 $116M 9
WVE Wave Life Sciences MetabolicNeurology+1 Rare 2 Phase 2 $665M 5
XNCR Xencor ImmunologyNeurology+1 Rare 1 Approved $2.68B 28
XENE Xenon Pharmaceuticals Neurology Rare 8 NDA Submitted $3.79B 9
XERS Xeris Biopharma MetabolicNeurology Rare 1 Approved $2.78B 4
ZBIO Zenas BioPharma DermatologyImmunology+2 Rare 3 NDA Submitted $1.92B 11