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Myotonic Dystrophy (4 companies)

Companies with an active program in Myotonic Dystrophy.

Ticker Company Therapeutic areas Programs Lead stage Mkt cap Programs
DYN Dyne Therapeutics MetabolicNeurology Rare 1 NDA Submitted $3.39B 10
HRMY Harmony Biosciences MetabolicNeurology Rare 1 Approved $1.94B 17
PEPG PepGen Neurology Rare 1 Phase 2 $171M 1
SRPT Sarepta Therapeutics NeurologyRespiratory Rare 1 Approved $1.91B 11