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Facioscapulohumeral Muscular Dystrophy (2 companies)

Companies with an active program in Facioscapulohumeral Muscular Dystrophy.

Ticker Company Therapeutic areas Programs Lead stage Programs
DYN Dyne Therapeutics, Inc. MetabolicNeurology Rare 1 Phase 3 10
SRPT Sarepta Therapeutics, Inc. Neurology Rare 1 Approved 10