Home › Therapeutic areas › Neurology › Facioscapulohumeral Muscular Dystrophy

Facioscapulohumeral Muscular Dystrophy (2 companies)

Companies with an active program in Facioscapulohumeral Muscular Dystrophy.

Ticker Company Therapeutic areas Programs Lead stage Mkt cap Programs
DYN Dyne Therapeutics MetabolicNeurology Rare 1 NDA Submitted $3.39B 10
SRPT Sarepta Therapeutics NeurologyRespiratory Rare 1 Approved $1.91B 11