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Facioscapulohumeral Muscular Dystrophy (2 companies)
Companies with an active program in Facioscapulohumeral Muscular Dystrophy.
| Ticker | Company | Therapeutic areas | Programs | Lead stage | Mkt cap | Programs |
|---|---|---|---|---|---|---|
| DYN | Dyne Therapeutics | MetabolicNeurology Rare | 1 | NDA Submitted | $3.39B | 10 |
| SRPT | Sarepta Therapeutics | NeurologyRespiratory Rare | 1 | Approved | $1.91B | 11 |
No companies match.