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Duchenne Muscular Dystrophy (9 companies)

Companies with an active program in Duchenne Muscular Dystrophy.

Ticker Company Therapeutic areas Programs Lead stage Mkt cap Programs
CAPR Capricor Therapeutics Infectious DiseaseNeurology Rare 1 NDA Submitted $523M 2
DYN Dyne Therapeutics MetabolicNeurology Rare 5 NDA Submitted $3.39B 10
INSM Insmed CardiovascularImmunology+3 Rare 1 Approved $25.1B 15
KROS Keros Therapeutics NeurologyOncology Rare 1 Phase 3 $184M 5
MESO Mesoblast CardiovascularGI/Hepatology+2 Rare 1 Approved $1.85B 5
DTIL Precision Biosciences Infectious DiseaseMetabolic+1 Rare 1 Phase 1 $296M 5
SRPT Sarepta Therapeutics NeurologyRespiratory Rare 4 Approved $1.91B 11
SLDB Solid Biosciences CardiovascularNeurology Rare 1 Phase 3 $736M 6
WVE Wave Life Sciences MetabolicNeurology+1 Rare 1 Phase 2 $665M 5