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Friedreich's Ataxia (4 companies)

Companies with an active program in Friedreich's Ataxia.

Ticker Company Therapeutic areas Programs Lead stage Mkt cap Programs
LRMR Larimar Therapeutics Neurology Rare 1 NDA Submitted $248M 1
LXEO Lexeo Therapeutics CardiovascularNeurology Rare 5 Phase 2 $237M 12
SLDB Solid Biosciences CardiovascularNeurology Rare 1 Phase 3 $736M 6
VYGR Voyager Therapeutics MetabolicNeurology Rare 1 Phase 1 $116M 9