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Amyotrophic Lateral Sclerosis (6 companies)

Companies with an active program in Amyotrophic Lateral Sclerosis.

Ticker Company Therapeutic areas Programs Lead stage Programs
AMLX Amylyx Pharmaceuticals, Inc. MetabolicNeurology Rare 1 Phase 3 5
ANNX Annexon, Inc. HematologyNeurologyOphthalmologyRenal Rare 1 NDA Submitted 6
CRVO CervoMed Inc. Neurology Rare 1 Phase 2 5
CLNN Clene Inc. Neurology Rare 1 NDA Submitted 5
QURE uniQure N.V. HematologyMetabolicNeurology Rare 1 Approved 6
VYGR Voyager Therapeutics, Inc. MetabolicNeurology Rare 1 Phase 1 7