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Amyotrophic Lateral Sclerosis (16 companies)

Companies with an active program in Amyotrophic Lateral Sclerosis.

Ticker Company Therapeutic areas Programs Lead stage Mkt cap Programs
AMLX Amylyx Pharmaceuticals MetabolicNeurology Rare 1 Phase 3 $3.79B 5
ANNX Annexon HematologyNeurology+2 Rare 1 Phase 3 $796M 6
CRVO CervoMed Neurology Rare 1 Phase 2 $21.5M 4
CLNN Clene Neurology Rare 1 NDA Submitted $56.9M 5
COYA Coya Therapeutics Neurology Rare 1 Phase 2 $70.1M 6
ELDN Eledon Pharmaceuticals ImmunologyMetabolic+1 Rare 1 Phase 2 $212M 3
INSM Insmed CardiovascularImmunology+3 Rare 1 Approved $25.1B 15
IONS Ionis Pharmaceuticals CardiovascularHematology+5 Rare 3 Approved $6.55B 29
KROS Keros Therapeutics NeurologyOncology Rare 1 Phase 3 $184M 5
MGTX MeiraGTx ImmunologyMetabolic+2 Rare 1 Phase 3 $864M 16
NRSN NeuroSense Therapeutics Neurology Rare 1 Phase 2 $3.2M 3
NRXP NRX Pharmaceuticals Neurology Rare 1 Approved $103M 7
KTTA Pasithea Therapeutics NeurologyOncology Rare 1 Phase 1 $19.3M 4
PMN ProMIS Neurosciences Neurology Rare 1 Phase 1 $37.3M 6
TLSA Tiziana Life Sciences ImmunologyNeurology Rare 1 Phase 2 $87.8M 5
VYGR Voyager Therapeutics MetabolicNeurology Rare 2 Phase 1 $116M 9