Biotech Distilled

Substack ↗ Subscribe

Subscribe Substack ↗ About

Research Areas Modalities Phases Targets Catalysts Track record Movers The Lead Compound

Home › Targets › UBE3A-AS

UBE3A-AS (1 companies · 1 programs)

Companies with an active program directed at UBE3A-AS.

Ultragenyx Pharmaceutical Inc. RARE

apazunersen — Angelman Syndrome Phase 3

Track record About Feedback Report a bug Substack ↗

This website is an encyclopedia of clinical-stage biotech companies, refreshed weekly. For informational and educational use only — not investment advice. Always verify against primary sources before making decisions.