Biotech Distilled
133 companies · 839 active programs
Substack ↗
Subscribe
Therapeutic Areas
Modalities
Phases
Targets
Companies
Home
›
Targets
› beta-glucuronidase
beta-glucuronidase
(1 companies · 1 programs)
Companies with an active program directed at beta-glucuronidase.
Ultragenyx Pharmaceutical Inc.
RARE
Mepsevii
— Mucopolysaccharidosis VII
Approved