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Sanfilippo Syndrome (1 companies)
Companies with an active program in Sanfilippo Syndrome.
| Ticker | Company | Therapeutic areas | Programs | Lead stage | Mkt cap | Programs |
|---|---|---|---|---|---|---|
| RARE | Ultragenyx Pharmaceutical | CardiovascularMetabolic+1 Rare | 1 | Approved | $1.57B | 10 |
No companies match.