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Glycogen Storage Disease Type Ia (2 companies)
Companies with an active program in Glycogen Storage Disease Type Ia.
| Ticker | Company | Therapeutic areas | Programs | Lead stage | Mkt cap | Programs |
|---|---|---|---|---|---|---|
| BEAM | Beam Therapeutics | HematologyMetabolic+1 Rare | 1 | Phase 2 | $2.73B | 6 |
| RARE | Ultragenyx Pharmaceutical | CardiovascularMetabolic+1 Rare | 1 | Approved | $1.57B | 10 |
No companies match.