Biotech Distilled
Substack ↗
Subscribe
Subscribe
Substack ↗
About
Research
Areas
Modalities
Phases
Targets
Catalysts
Filings
Track record
Movers
The Lead Compound
Home
›
Targets
› SCN1A
SCN1A
(1 companies · 1 programs)
Companies with an active program directed at SCN1A.
Stoke Therapeutics, Inc.
STOK
zorevunersen
— Dravet Syndrome
Phase 3