Sarepta Therapeutics, Inc. SRPT
- SRP-1005 — Huntington's Disease Phase 1
huntingtin (2 companies · 2 programs)
Companies with an active program directed at huntingtin.
uniQure N.V. QURE
- ifezuntirgene inilparvovec — Huntington's Disease NDA Submitted
Companies with an active program directed at huntingtin.