Biotech Distilled
133 companies · 839 active programs
Substack ↗
Subscribe
Therapeutic Areas
Modalities
Phases
Targets
Companies
Home
›
Targets
› exon 53
exon 53
(1 companies · 1 programs)
Companies with an active program directed at exon 53.
Dyne Therapeutics, Inc.
DYN
DYNE-253
— Duchenne Muscular Dystrophy
Preclinical