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133 companies · 839 active programs
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› DMPK
DMPK
(2 companies · 2 programs)
Companies with an active program directed at DMPK.
Dyne Therapeutics, Inc.
DYN
zeleciment basivarsen
— Myotonic Dystrophy Type 1
Phase 1
Sarepta Therapeutics, Inc.
SRPT
SRP-1003
— Myotonic Dystrophy Type 1
Phase 1