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beta-sarcoglycan (1 companies · 2 programs)

Companies with an active program directed at beta-sarcoglycan.

Sarepta Therapeutics, Inc. SRPT

  • bidridistrogene xeboparvovec — Limb-Girdle Muscular Dystrophy Phase 3
  • SRP-9004 — Limb-Girdle Muscular Dystrophy Phase 1