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Nucleic Acid (16 companies)

Ticker Company Therapeutic areas Programs Lead stage Mkt cap Programs
AGIO Agios Pharmaceuticals HematologyMetabolic Rare 1 Approved $1.76B 7
AMLX Amylyx Pharmaceuticals MetabolicNeurology Rare 1 Phase 3 $3.79B 5
BEAM Beam Therapeutics HematologyMetabolic+1 Rare 3 Phase 2 $2.73B 6
DYN Dyne Therapeutics MetabolicNeurology Rare 9 NDA Submitted $3.39B 10
ELTX Elicio Therapeutics Oncology 1 Phase 2 $42.7M 6
GERN Geron Oncology 3 Approved $638M 3
IONS Ionis Pharmaceuticals CardiovascularHematology+5 Rare 28 Approved $6.55B 29
LXEO Lexeo Therapeutics CardiovascularNeurology Rare 1 Phase 2 $237M 12
PEPG PepGen Neurology Rare 1 Phase 2 $171M 1
PHIO Phio Pharmaceuticals Oncology 4 Phase 1 $9.6M 4
PRQR ProQR Therapeutics MetabolicNeurology Rare 7 Phase 1 $191M 7
SRPT Sarepta Therapeutics NeurologyRespiratory Rare 9 Approved $1.91B 11
STOK Stoke Therapeutics Neurology Rare 2 Phase 3 $1.74B 2
HURA TuHURA Biosciences Oncology 3 Phase 3 $104M 4
VNDA Vanda Pharmaceuticals CardiovascularDermatology+6 Rare 3 Approved $231M 27
WVE Wave Life Sciences MetabolicNeurology+1 Rare 5 Phase 2 $665M 5