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Alpha-1 Antitrypsin Deficiency (3 companies)
Companies with an active program in Alpha-1 Antitrypsin Deficiency.
| Ticker | Company | Therapeutic areas | Programs | Lead stage | Mkt cap | Programs |
|---|---|---|---|---|---|---|
| FDMT | 4D Molecular Therapeutics | OphthalmologyRespiratory Rare | 1 | Phase 3 | $677M | 5 |
| BEAM | Beam Therapeutics | HematologyMetabolic+1 Rare | 1 | Phase 2 | $2.73B | 6 |
| WVE | Wave Life Sciences | MetabolicNeurology+1 Rare | 1 | Phase 2 | $665M | 5 |
No companies match.