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Alpha-1 Antitrypsin Deficiency (2 companies)

Companies with an active program in Alpha-1 Antitrypsin Deficiency.

Ticker Company Therapeutic areas Programs Lead stage Programs
BEAM Beam Therapeutics Inc. HematologyMetabolicRespiratory Rare 1 Phase 1 8
WVE Wave Life Sciences Ltd. MetabolicNeurologyRespiratory Rare 1 Phase 2 5