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Phenylketonuria (4 companies)

Companies with an active program in Phenylketonuria.

Ticker Company Therapeutic areas Programs Lead stage Mkt cap Programs
AGIO Agios Pharmaceuticals HematologyMetabolic Rare 1 Approved $1.76B 7
BEAM Beam Therapeutics HematologyMetabolic+1 Rare 1 Phase 2 $2.73B 6
ETON Eton Pharmaceuticals GI/HepatologyInfectious Disease+3 Rare 1 Approved $1.63B 17
MAZE Maze Therapeutics MetabolicRenal Rare 1 Phase 2 $1.90B 4