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Bardet-Biedl Syndrome (2 companies)
Companies with an active program in Bardet-Biedl Syndrome.
| Ticker | Company | Therapeutic areas | Programs | Lead stage | Programs |
|---|---|---|---|---|---|
| MGTX | MeiraGTx | ImmunologyMetabolic+2 Rare | 2 | Phase 2 | 16 |
| RYTM | Rhythm Pharmaceuticals | Metabolic Rare | 1 | Approved | 13 |
No companies match.